Advanced gene therapy resources
We develop gene therapies using CRISPR/Cas9 to correct mutations, working towards safe and effective therapeutic applications for human genetic diseases that do not yet have medical alternatives
We develop gene therapies using CRISPR/Cas9 to correct mutations, working towards safe and effective therapeutic applications for human genetic diseases that do not yet have medical alternatives
Advanced gene therapy resources Home /Recursos avançados em terapia… Gene therapy is part of an innovative class of treatments known as advanced therapy medicinal products (ATMPs), which has been developing internationally for over a decade and has demonstrated scientific and technological advances that are favorable for treating hematological and ocular diseases and some types of…